People with sickle cell disease experience excruciating pain crises, tissue and organ damage, and shortened life expectancy. The lab of Stuart Orkin made crucial discoveries that, in the hands of CRISPR Therapeutics and Vertex Pharmaceuticals, became an FDA-approved gene therapy that is making a monumental impact on patients with sickle cell disease.
Related Posts
Why 'Good Enough' AI May Suit Health Systems Better
October 26, 2026
IBM's CEO says open weight models now deliver about 90% of frontier performance at far lower cost on-prem. Here's what that tradeoff means for healthcare.
Why DR Congo's Ebola Outbreak Is So Hard to Contain
October 19, 2026
Ebola has reached an eighth province in DR Congo. Here is why this Bundibugyo outbreak is so hard to stop, and what it shows about outbreak response.
AI Is Less Regulated Than Milk: What That Means for Health Care
October 12, 2026
Microsoft's Brad Smith says AI is less regulated than milk. Here's what that safety gap could mean for patients and the health care tools they rely on.
Why Endangered Trapdoor Spiders Are Key to Conservation Success
October 5, 2026
Explore how studying endangered trapdoor spiders can reveal vital insights into conservation efforts and ecosystem resilience.